Let's check out two exciting biotech stocks that may climb 58% and 200%, according to Wall Street. Image source: Getty Images ...
The company could finally be ready to deliver on years of promise.
A sales partner offered a ray of hope that this company couldn't for itself.
Dr. Rebecca Ahrens-Nicklas and Dr. Kiran Musunru crafted a bespoke treatment that has successfully corrected the genetic defect.
Vertex executives warned that Casgevy, its curative treatment for sickle cell disease, would be slow to reach patients. But ...
Nicole and Kyle Muldoon with their child, KJ, who received a CRISPR gene editing therapy at Children's Hospital of Philadelphia. From the San Francisco Business Times. Months after helping manufacture ...
The recent clinical success of treating “Baby KJ” Muldoon—an infant born with a rare metabolic disease—with the first-ever personalized gene-editing therapy brought much-needed enthusiasm to the ...
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New Jersey man says CRISPR treatment for sickle cell disease changed his life: "It totally worked"
Austin Louis, 20, says the CRISPR treatment he received at the Children's Hospital of Philadelphia for sickle cell disease ...
In a keynote talk during GEN’s “The State of CRISPR & Genome Editing” virtual summit, originally broadcast on June 11, 2025, Fyodor Urnov, PhD, Director, Technology & Translation, Innovative Genomics ...
Rare genetic diseases are challenging for patients and their families—made all the more overwhelming because symptoms tend to appear soon after birth. To date, there haven’t been many reliable ...
The idea of self-amplifying gene editing is to get cells to pass on packages of CRISPR machinery to their neighbours, boosting the effect ...
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